{"database":"biostudies-literature","file_versions":[],"scores":null,"additional":{"omics_type":["Unknown"],"volume":["207(6)"],"submitter":["Nowak D"],"funding":["German Research Foundation","Health + Life Science Alliance Heidelberg Mannheim","Deutsche Forschungsgemeinschaft","Dr. Werner Jackstädt-Stiftung","Bundesinstitut für Risikobewertung","Torsten Haferlach Leukämiediagnostik Stiftung","Deutsche Krebshilfe","Forum Gesundheitsstandort Baden-Württemberg","Medical Faculty Mannheim, Heidelberg University"],"journal":["British journal of haematology"],"pagination":["2558-2562"],"full_dataset_link":["https://www.ebi.ac.uk/biostudies/studies/S-EPMC12710189"],"repository":["biostudies-literature"],"pubmed_title":["Primary CD34&lt;sup&gt;+&lt;/sup&gt; cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243."],"pmcid":["PMC12710189"],"funding_grant_id":["60‐0102‐01.P638‐12710524","143/235/80937","SFB 1709/1 2025—533056198","SFB 1709/1 2025-533056198","MWK32-7531-26/8/2","60-0102-01.P638-12710524","BW 4-5400/136/1","70113953"],"pubmed_authors":["Klink T","Palme I","Darwich A","Metzgeroth G","Klar A","Hahn M","Oblander J","Schmitt N","Belzer AC","Rapp F","Gol M","Nowak D","Demmerle M","Abba M","Hofmann F","Weimer N","Altrock E","Streuer A","Riabov V","Hofmann WK","Steiner L","Nowak V"],"additional_accession":[]},"is_claimable":false,"name":"Primary CD34&lt;sup&gt;+&lt;/sup&gt; cells of patients with vacuoles, E1 enzyme, X-linked, autoinflammatory, somatic (VEXAS) syndrome are highly sensitive to targeted treatment with TAK-243.","description":null,"dates":{"release":"2025-01-01T00:00:00Z","publication":"2025 Dec","modification":"2026-06-07T05:07:06.945Z","creation":"2026-06-07T03:07:07.88Z"},"accession":"S-EPMC12710189","cross_references":{"pubmed":["41077698"],"doi":["10.1111/bjh.70203"]}}