{"database":"biostudies-literature","file_versions":[],"scores":null,"additional":{"omics_type":["Unknown"],"volume":["68(6)"],"submitter":["Tucci F"],"funding":["Telethon"],"journal":["Hepatology (Baltimore, Md.)"],"pagination":["2434-2437"],"full_dataset_link":["https://www.ebi.ac.uk/biostudies/studies/S-EPMC6588006"],"repository":["biostudies-literature"],"pubmed_title":["Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis."],"pmcid":["PMC6588006"],"funding_grant_id":["TGT16S01"],"pubmed_authors":["Casiraghi M","Consiglieri G","Barzaghi F","Aiuti A","Calbi V","Ciceri F","Marktel S","Recupero S","Gabaldo M","Appleby J","Bernardo ME","Mieli-Vergani G","Migliavacca M","Cestone E","Lucano C","Darin S","Dionisio F","Calzatini F","Finazzi R","Canarutto D","Abd Elaziz D","Cicalese MP","Tucci F","Ferrua F","Boeri E"],"additional_accession":[]},"is_claimable":false,"name":"Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis.","description":null,"dates":{"release":"2018-01-01T00:00:00Z","publication":"2018 Dec","modification":"2025-04-21T17:21:20.501Z","creation":"2025-04-05T16:22:52.25Z"},"accession":"S-EPMC6588006","cross_references":{"pubmed":["30014500"],"doi":["10.1002/hep.30160"]}}