<HashMap><database>biostudies-literature</database><scores/><additional><omics_type>Unknown</omics_type><volume>68(6)</volume><submitter>Tucci F</submitter><funding>Telethon</funding><journal>Hepatology (Baltimore, Md.)</journal><pagination>2434-2437</pagination><full_dataset_link>https://www.ebi.ac.uk/biostudies/studies/S-EPMC6588006</full_dataset_link><repository>biostudies-literature</repository><pubmed_title>Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis.</pubmed_title><pmcid>PMC6588006</pmcid><funding_grant_id>TGT16S01</funding_grant_id><pubmed_authors>Casiraghi M</pubmed_authors><pubmed_authors>Consiglieri G</pubmed_authors><pubmed_authors>Barzaghi F</pubmed_authors><pubmed_authors>Aiuti A</pubmed_authors><pubmed_authors>Calbi V</pubmed_authors><pubmed_authors>Ciceri F</pubmed_authors><pubmed_authors>Marktel S</pubmed_authors><pubmed_authors>Recupero S</pubmed_authors><pubmed_authors>Gabaldo M</pubmed_authors><pubmed_authors>Appleby J</pubmed_authors><pubmed_authors>Bernardo ME</pubmed_authors><pubmed_authors>Mieli-Vergani G</pubmed_authors><pubmed_authors>Migliavacca M</pubmed_authors><pubmed_authors>Cestone E</pubmed_authors><pubmed_authors>Lucano C</pubmed_authors><pubmed_authors>Darin S</pubmed_authors><pubmed_authors>Dionisio F</pubmed_authors><pubmed_authors>Calzatini F</pubmed_authors><pubmed_authors>Finazzi R</pubmed_authors><pubmed_authors>Canarutto D</pubmed_authors><pubmed_authors>Abd Elaziz D</pubmed_authors><pubmed_authors>Cicalese MP</pubmed_authors><pubmed_authors>Tucci F</pubmed_authors><pubmed_authors>Ferrua F</pubmed_authors><pubmed_authors>Boeri E</pubmed_authors></additional><is_claimable>false</is_claimable><name>Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis.</name><description/><dates><release>2018-01-01T00:00:00Z</release><publication>2018 Dec</publication><modification>2025-04-21T17:21:20.501Z</modification><creation>2025-04-05T16:22:52.25Z</creation></dates><accession>S-EPMC6588006</accession><cross_references><pubmed>30014500</pubmed><doi>10.1002/hep.30160</doi></cross_references></HashMap>