ENAapplication/xmlftp.sra.ebi.ac.uk/vol1/fastq/SRR103/086/SRR10382486/SRR10382486_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/072/SRR10382472/SRR10382472_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/044/SRR10382444/SRR10382444_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/068/SRR10382468/SRR10382468_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/062/SRR10382462/SRR10382462_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/031/SRR10382431/SRR10382431_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/090/SRR10382490/SRR10382490_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/061/SRR10382461/SRR10382461_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/055/SRR10382455/SRR10382455_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/069/SRR10382469/SRR10382469_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/079/SRR10382479/SRR10382479_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/085/SRR10382485/SRR10382485_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/045/SRR10382445/SRR10382445_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/029/SRR10382429/SRR10382429_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/088/SRR10382488/SRR10382488_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/043/SRR10382443/SRR10382443_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/042/SRR10382442/SRR10382442_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/057/SRR10382457/SRR10382457_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/028/SRR10382428/SRR10382428_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/081/SRR10382481/SRR10382481_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/040/SRR10382440/SRR10382440_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/034/SRR10382434/SRR10382434_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/033/SRR10382433/SRR10382433_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/049/SRR10382449/SRR10382449_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/087/SRR10382487/SRR10382487_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/058/SRR10382458/SRR10382458_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/073/SRR10382473/SRR10382473_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/067/SRR10382467/SRR10382467_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/066/SRR10382466/SRR10382466_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/064/SRR10382464/SRR10382464_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/063/SRR10382463/SRR10382463_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/064/SRR10382464/SRR10382464_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/052/SRR10382452/SRR10382452_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/076/SRR10382476/SRR10382476_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/037/SRR10382437/SRR10382437_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/066/SRR10382466/SRR10382466_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/078/SRR10382478/SRR10382478_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/081/SRR10382481/SRR10382481_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/049/SRR10382449/SRR10382449_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/040/SRR10382440/SRR10382440_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/030/SRR10382430/SRR10382430_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/042/SRR10382442/SRR10382442_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/054/SRR10382454/SRR10382454_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/048/SRR10382448/SRR10382448_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/039/SRR10382439/SRR10382439_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/088/SRR10382488/SRR10382488_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/091/SRR10382491/SRR10382491_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/036/SRR10382436/SRR10382436_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/058/SRR10382458/SRR10382458_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/082/SRR10382482/SRR10382482_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/070/SRR10382470/SRR10382470_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/051/SRR10382451/SRR10382451_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/063/SRR10382463/SRR10382463_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/060/SRR10382460/SRR10382460_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/072/SRR10382472/SRR10382472_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/034/SRR10382434/SRR10382434_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/075/SRR10382475/SRR10382475_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/087/SRR10382487/SRR10382487_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/084/SRR10382484/SRR10382484_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/046/SRR10382446/SRR10382446_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/037/SRR10382437/SRR10382437_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/028/SRR10382428/SRR10382428_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/084/SRR10382484/SRR10382484_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/029/SRR10382429/SRR10382429_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/074/SRR10382474/SRR10382474_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/056/SRR10382456/SRR10382456_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/050/SRR10382450/SRR10382450_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/043/SRR10382443/SRR10382443_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/071/SRR10382471/SRR10382471_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/067/SRR10382467/SRR10382467_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/073/SRR10382473/SRR10382473_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/057/SRR10382457/SRR10382457_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/033/SRR10382433/SRR10382433_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/032/SRR10382432/SRR10382432_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/054/SRR10382454/SRR10382454_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/031/SRR10382431/SRR10382431_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/030/SRR10382430/SRR10382430_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/090/SRR10382490/SRR10382490_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/079/SRR10382479/SRR10382479_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/051/SRR10382451/SRR10382451_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/045/SRR10382445/SRR10382445_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/085/SRR10382485/SRR10382485_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/091/SRR10382491/SRR10382491_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/039/SRR10382439/SRR10382439_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/055/SRR10382455/SRR10382455_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/070/SRR10382470/SRR10382470_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/078/SRR10382478/SRR10382478_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/052/SRR10382452/SRR10382452_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/046/SRR10382446/SRR10382446_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/076/SRR10382476/SRR10382476_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/075/SRR10382475/SRR10382475_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/069/SRR10382469/SRR10382469_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/061/SRR10382461/SRR10382461_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/060/SRR10382460/SRR10382460_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/048/SRR10382448/SRR10382448_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/082/SRR10382482/SRR10382482_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/036/SRR10382436/SRR10382436_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/089/SRR10382489/SRR10382489_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/053/SRR10382453/SRR10382453_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/065/SRR10382465/SRR10382465_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/038/SRR10382438/SRR10382438_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/041/SRR10382441/SRR10382441_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/077/SRR10382477/SRR10382477_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/080/SRR10382480/SRR10382480_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/089/SRR10382489/SRR10382489_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/047/SRR10382447/SRR10382447_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/065/SRR10382465/SRR10382465_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/083/SRR10382483/SRR10382483_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/041/SRR10382441/SRR10382441_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/077/SRR10382477/SRR10382477_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/071/SRR10382471/SRR10382471_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/059/SRR10382459/SRR10382459_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/053/SRR10382453/SRR10382453_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/080/SRR10382480/SRR10382480_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/035/SRR10382435/SRR10382435_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/062/SRR10382462/SRR10382462_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/038/SRR10382438/SRR10382438_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/068/SRR10382468/SRR10382468_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/050/SRR10382450/SRR10382450_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/056/SRR10382456/SRR10382456_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/059/SRR10382459/SRR10382459_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/035/SRR10382435/SRR10382435_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/074/SRR10382474/SRR10382474_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/086/SRR10382486/SRR10382486_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/083/SRR10382483/SRR10382483_1.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/047/SRR10382447/SRR10382447_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/044/SRR10382444/SRR10382444_2.fastq.gzftp.sra.ebi.ac.uk/vol1/fastq/SRR103/032/SRR10382432/SRR10382432_2.fastq.gzprimaryOK200GenomicsShanghai Jiao Tong University School of Medicinehttps://www.ebi.ac.uk/ena/browser/view/PRJNA587051Agxt off-target, Hao1 on/off-targetENATherapy, Genetic Therapy, primary hyperoxaluria caused by mutation in AGXT, Somatic, peroxisomal alanine:glyoxylate aminotransferase deficiency, type 1, hyperoxaluria, peroxisomal alanine glyoxylate aminotransferase deficiency, Gametic Genetic, Genetic, Somatic Genetic Therapies, Somatic Gene Therapy, Gametic Genetic Therapies, DNA Therapy, primary hyperoxaluria type 1, hepatic AGT deficiency, Gene, Somatic Gene, peroxisomal alanine-glyoxylate aminotransferase deficiency, Somatic Genetic Therapy, AGXT primary hyperoxaluria, Somatic Genetic, Genetic Therapies, Gene Therapy, serine:pyruvate aminotransferase deficiency, HP1, type I, Gametic, Gametic Genetic Therapy., Therapies, Oxalosis 1, glycolic aciduria, primary hyperoxaluria type I, DNA, PH1, serine pyruvate aminotransferase deficiency, alanine-glyoxylate aminotransferase deficiency, primary0.00.00.00.00.0falseNGS for PH1 gene therapy2022-05-122020-06-07PRJNA58705110116