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Jiao Tong University School of Medicine</center_name><full_dataset_link>https://www.ebi.ac.uk/ena/browser/view/PRJNA828129</full_dataset_link><long_description>NGS data of using Cpf1 to treat PH1</long_description><repository>ENA</repository><description_synonyms>peroxisomal alanine:glyoxylate aminotransferase deficiency, type 1, hyperoxaluria, peroxisomal alanine glyoxylate aminotransferase deficiency, serine:pyruvate aminotransferase deficiency, CPF1, HP1, type I, hepatic AGT deficiency, Oxalosis 1, CEP1., serine pyruvate aminotransferase deficiency, alanine-glyoxylate aminotransferase deficiency, primary</description_synonyms></additional><is_claimable>false</is_claimable><name></name><description>Treat PH1 with Cpf1</description><dates><last_updated>2023-05-17</last_updated><first_public>2022-04-25</first_public></dates><accession>PRJNA828129</accession><cross_references/></HashMap>