AAV-vectored base editor trans-splicing delivers dystrophin repair.
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ABSTRACT:
SUBMITTER: Li Z
PROVIDER: S-EPMC10280080 | biostudies-literature | 2023 Jun
REPOSITORIES: biostudies-literature
Publications
AAV-vectored base editor <i>trans</i>-splicing delivers dystrophin repair.
Li Zhen Z Gonçalves Manuel A F V MAFV
Molecular therapy. Nucleic acids 20230530
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