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Dataset Information

S264: EDIT-301 SHOWS PROMISING PRELIMINARY SAFETY AND EFFICACY RESULTS IN THE PHASE I/II CLINICAL TRIAL (RUBY) OF PATIENTS WITH SEVERE SICKLE CELL DISEASE USING HIGHLY SPECIFIC AND EFFICIENT ASCAS12A ENZYME


ABSTRACT:

SUBMITTER: Hanna R 

PROVIDER: S-EPMC10428233 | biostudies-literature | 2023 Aug

REPOSITORIES: biostudies-literature