Desmopressin in nonsevere hemophilia A: patient perspectives on use and efficacy.

ABSTRACT:

Background

Desmopressin increases plasma factor VIII and von Willebrand factor levels in persons with nonsevere hemophilia A. Patients' perspectives on desmopressin are relevant to increase and optimize its suboptimal use. However, patients' views on desmopressin are not reported.

Objectives

To evaluate the perspectives of persons with nonsevere hemophilia A on desmopressin use, barriers for its use, side effects, and their knowledge about desmopressin's efficacy and side effects.

Methods

Persons with nonsevere hemophilia A were included in a cross-sectional, national, multicenter study. Questionnaires were filled out by adult patients and children aged ≥12 years themselves. Caretakers filled out questionnaires for children aged <12 years.

Results

In total, 706

SUBMITTER: Romano LGR 

PROVIDER: S-EPMC10439392 | biostudies-literature | 2023 Jul

REPOSITORIES: biostudies-literature