The Rare Diseases Clinical Research Network: a model for clinical trial readiness.

ABSTRACT:

Background

The current road to developing treatments for rare diseases is often slow, expensive, and riddled with risk. Change is needed to improve the process, both in how we think about rare disease treatment development and the infrastructure we build to support ongoing science. The National Institutes of Health (NIH)-supported Rare Diseases Clinical Research Network (RDCRN) was established to advance the diagnosis, management, and treatment of rare diseases and to promote highly collaborative, multi-site, patient-centric, translational, and clinical research. The current iteration of the RDCRN intends to build upon and enhance successful approaches within the network while identifying innovative methods to fill gaps and address needs in the approach to the rare disease treatmen

SUBMITTER: Lumsden JM 

PROVIDER: S-EPMC10752072 | biostudies-literature | 2023 Jan-Dec

REPOSITORIES: biostudies-literature