Health care costs of home care enzyme replacement therapy for patients with lysosomal storage diseases in Germany.

ABSTRACT:

Background

Lysosomal storage diseases (LSDs) can be treated with intravenous enzyme replacement therapy (ERT). ERT is being administered either in specialized clinics or in the home care setting. Studies indicate that home-based ERT can be considered safe and positively effects patient reported outcomes. Due to the higher level of individual care required by nurses when administering ERT at home, questions arise whether this will result in additional costs for health care systems. Since cost data to the German health care system are currently unavailable, this study aims to assess home care ERT costs of LSD patients.

Methods

The longitudinal study assessed the direct costs of home-based ERT for patients with LSD diseases Fabry, Pompe, Gaucher, and MPS I from 2019 to 2021 on

SUBMITTER: Heinrich R 

PROVIDER: S-EPMC11648283 | biostudies-literature | 2024 Dec

REPOSITORIES: biostudies-literature