Real-World Unmet Needs of Patients With Haemophilia A and Haemophilia B With or Without Inhibitors: End-of-Study Results From the explorer6 Non-Interventional Study.

ABSTRACT:

Introduction

Haemophilia is associated with high disease and treatment burdens. Prospective evaluation of data from patients with haemophilia helps understand and define unmet needs, optimise treatment and improve healthcare outcomes.

Aim

To present end-of-study data from explorer6 (NCT03741881), a prospective, non-interventional study across multiple countries in patients with haemophilia (haemophilia A or B without [HA or HB] or with inhibitors [HAwI or HBwI]).

Methods

Patients ≥12 years old with severe HA, severe/moderate HB or HAwI/HBwI of any severity were treated according to the local standard of care (SoC). The number of bleeding episodes from enrolment up to a maximum of 115 weeks, physical activity based on data collected by a wrist-worn physical activity tr

SUBMITTER: Wheeler AP 

PROVIDER: S-EPMC12462599 | biostudies-literature | 2025 Sep

REPOSITORIES: biostudies-literature