Clinical, humanistic, and economic burden of haemophilia A in China: findings from a real-world survey.

ABSTRACT:

Objectives

We aimed to describe current treatments for haemophilia A in China, focusing on their associated clinical, humanistic, and economic burdens in a real-world context.

Methods

This was a retrospective cross-sectional study. We investigated the demographics, disease severity, treatment strategies, and clinical outcomes of patients diagnosed with haemophilia A. We also investigated the cost of the treatment of patients with haemophilia A. In the real world, we estimated annual direct medical costs, direct non-medical costs and indirect costs. In addition, we employed the EQ-5D and SF-6D to measure the humanistic burden of patients.

Results

A total of 60 patients were included in the study, comprising 22 children (< 18 years) and 38 adults (≥ 18 years). The mean

SUBMITTER: Feng J 

PROVIDER: S-EPMC12551187 | biostudies-literature | 2025 Oct

REPOSITORIES: biostudies-literature