Intrathecal idursulfase‐IT in children younger than 3 years with neuronopathic mucopolysaccharidosis II in a single‐arm, open‐label, phase 2/3 substudy and extension

ABSTRACT:

SUBMITTER: Muenzer J 

PROVIDER: S-EPMC12928010 | biostudies-literature | 2026 Feb

REPOSITORIES: biostudies-literature