The burden of Duchenne muscular dystrophy: an international, cross-sectional study.

ABSTRACT:

Objective

The objective of this study was to estimate the total cost of illness and economic burden of Duchenne muscular dystrophy (DMD).

Methods

Patients with DMD from Germany, Italy, United Kingdom, and United States were identified through Translational Research in Europe-Assessment & Treatment of Neuromuscular Diseases registries and invited to complete a questionnaire online together with a caregiver. Data on health care use, quality of life, work status, informal care, and household expenses were collected to estimate costs of DMD from the perspective of society and caregiver households.

Results

A total of 770 patients (173 German, 122 Italian, 191 from the United Kingdom, and 284 from the United States) completed the questionnaire. Mean per-patient annual direc

SUBMITTER: Landfeldt E 

PROVIDER: S-EPMC4141999 | biostudies-literature | 2014 Aug

REPOSITORIES: biostudies-literature