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Hard targets for a second skeleton: therapeutic horizons for fibrodysplasia ossificans progressiva (FOP).


ABSTRACT:

SUBMITTER: Kaplan FS 

PROVIDER: S-EPMC5697787 | biostudies-literature | 2017

REPOSITORIES: biostudies-literature

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Hard targets for a second skeleton: therapeutic horizons for fibrodysplasia ossificans progressiva (FOP).

Kaplan Frederick S FS   Pignolo Robert J RJ   Al Mukaddam Mona M MM   Shore Eileen M EM  

Expert opinion on orphan drugs 20170317 4


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