S-EPMC6119153 - Short-hairpin RNA against aberrant <i>HBB</i><sup>IVSI-110(G>A)</sup> mRNA restores β-globin levels in a novel cell model and acts as mono- and combination therapy for β-thalassemia in primary hematopoietic stem cells. - OmicsDI

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Dataset Information

Short-hairpin RNA against aberrant HBB^{IVSI-110(G>A)} mRNA restores β-globin levels in a novel cell model and acts as mono- and combination therapy for β-thalassemia in primary hematopoietic stem cells.

ABSTRACT:

SUBMITTER: Patsali P

PROVIDER: S-EPMC6119153 | biostudies-literature | 2018 Sep

REPOSITORIES: biostudies-literature