Producing a preference-based quality of life measure for people with Duchenne muscular dystrophy: a mixed-methods study protocol.

ABSTRACT:

Introduction

Preference-based measures (PBMs) of health-related quality of life (HRQoL) are used to generate quality-adjusted life years, which are necessary for cost-effectiveness evaluations of health interventions via cost-utility analysis. These measures of health can be generic (ie, pandiagnostic) or condition specific. No condition-specific PBM of HRQoL in Duchenne muscular dystrophy (DMD) exists, yet there are concerns that standard generic measures lack the specificity to assess aspects of HRQoL that are especially important to people with DMD. This study has been designed to produce a condition-specific PBM of HRQoL in DMD.

Methods and analysis

This mixed-methods study proceeds through three stages. In the first stage (concept elicitation), semistructured interviews

SUBMITTER: Powell PA 

PROVIDER: S-EPMC6429747 | biostudies-literature | 2019 Mar

REPOSITORIES: biostudies-literature