Ontology highlight
ABSTRACT: Background
Myotonic dystrophy (DM) is a rare, inherited disorder with multi-systemic effects that impact the skeletal muscles, eyes, heart, skin and gastrointestinal, endocrine, respiratory, and central nervous systems. DM is divided into two subtypes: DM1 can present from early childhood through adulthood and also has a congenital form (cDM) while DM2 typically manifests during mid-adulthood. Both forms are progressive with no approved treatments, and unmet need for disease-modifying therapies remains high. This study interrogated health insurance claims data to explore the clinical experience, healthcare resource utilization (HCRU), and all-cause costs for DM.Results
A total of 8541 patients with DM and 242 patients with cDM and their matched controls were selected from a
SUBMITTER: Howe SJ
PROVIDER: S-EPMC8867662 | biostudies-literature | 2022 Feb
REPOSITORIES: biostudies-literature