The State of Patient-Reported Outcome Measures for Pediatric Patients with Inherited Retinal Disease.

ABSTRACT: Patient-reported outcome measures (PROMs) are questionnaires that assess health outcomes meaningful to the patient. PROMs have multiple applications, such as supporting clinicians' decision-making for patient care, understanding the impact of disease on patient functioning, and evaluating the efficacy of therapeutics. Though PROMs were developed for various eye conditions, no PROM was tailored to pediatric patients with inherited retinal disease (IRD). Hence, a literature search was conducted using MEDLINE and Embase to identify PROMs potentially relevant to this patient population. This review evaluated selected pediatric PROMs against the US Food and Drug Administration (FDA) guidelines and found restricted use in the context of IRD. As there is a need for PROMs tailored to pediatric pat

SUBMITTER: Selvan K 

PROVIDER: S-EPMC9114271 | biostudies-literature | 2022 Jun

REPOSITORIES: biostudies-literature