Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD.
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ABSTRACT:
SUBMITTER: Schwartz JD
PROVIDER: S-EPMC9305868 | biostudies-literature | 2022 Mar
REPOSITORIES: biostudies-literature
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Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD.
Schwartz Jonathan D JD Barcellini Wilma W Grace Rachel F RF Bianchi Paola P Zanella Alberto A López Lorenzo José Luis JL Sevilla Julián J Shah Ami J AJ Glader Bertil B Nicoletti Eileen E Navarro Ordoñez Susana S Segovia José Carlos JC
American journal of hematology 20220124 3
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