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Restored Hematopoietic Stem Cell Transcriptional Program in Fanconi Anemia Patients Following Gene Therapy

ABSTRACT: The effect of gene therapy in the Hematopoietic stem cells of patients with fanconi anemia has been analyzed. For this purpose 3 fanconi patients bone marrow and a healthy one has been aspirated and CD34+ cells sorted. The data was processed using the usual 10X protocol

ORGANISM(S): Homo sapiens

PROVIDER: GSE180536 | GEO | 2023/04/12

REPOSITORIES: GEO

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