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2022
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CRISPR medicine for blood disorders: Progress and challenges in delivery.
Not available
S-EPMC9853164
|
biostudies-literature
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Somatic Reversion of a Novel IL2RG Mutation Resulting in Atypical X-Linked Combined Immunodeficiency.
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S-EPMC8774591
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biostudies-literature
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Challenges in Gene Therapy for Somatic Reverted Mosaicism in X-Linked Combined Immunodeficiency by CRISPR/Cas9 and Prime Editing.
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S-EPMC9777626
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biostudies-literature
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Preclinical Evaluation of CRISPR-Edited CAR-NK-92 Cells for Off-the-Shelf Treatment of AML and B-ALL.
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S-EPMC9655234
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biostudies-literature
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Sugar transporters for intercellular exchange and nutrition of pathogens.
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S-EPMC3000469
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biostudies-literature
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Quantitative definition of neurobehavior, vision, hearing and brain volumes in macaques congenitally exposed to Zika virus.
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S-EPMC7580995
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biostudies-literature
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TCTEX1D2 mutations underlie Jeune asphyxiating thoracic dystrophy with impaired retrograde intraflagellar transport.
Not available
S-EPMC4468853
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biostudies-literature
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