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2024
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2023
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2020
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A juvenile-onset, progressive cataract locus on chromosome 3q21-q22 is associated with a missense mutation in the beaded filament structural protein-2.
Not available
S-EPMC1288209
|
biostudies-literature
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Preclinical Evaluation of ADVM-022, a Novel Gene Therapy Approach to Treating Wet Age-Related Macular Degeneration.
Not available
S-EPMC6319194
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biostudies-literature
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Structure comparison of the chimeric AAV2.7m8 vector with parental AAV2.
Not available
S-EPMC7058502
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biostudies-literature
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Acetylcholine receptor based chemogenetics engineered for neuronal inhibition and seizure control assessed in mice.
Not available
S-EPMC10796428
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biostudies-literature
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Matrix metalloproteinase-3 (MMP-3)-mediated gene therapy for glaucoma.
Not available
S-EPMC10115410
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biostudies-literature
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