Sort   by:  
 Page size 
UnknownHSPB1 mutations causing hereditary neuropathy in humans disrupt non-cell autonomous protection of motor neurons.
Not available
S-EPMC5612892 | biostudies-literature
UnknownVoluntary wheel running with and without follistatin overexpression improves NMJ transmission but not motor unit loss in late life of C57BL/6J mice.
Not available
S-EPMC8122043 | biostudies-literature
UnknownElectrophysiological Biomarkers in Spinal Muscular Atrophy: Preclinical Proof of Concept.
Not available
S-EPMC3914317 | biostudies-literature
UnknownMajor histocompatibility complex class I molecules protect motor neurons from astrocyte-induced toxicity in amyotrophic lateral sclerosis.
Not available
S-EPMC4823173 | biostudies-literature
UnknownImproving single injection CSF delivery of AAV9-mediated gene therapy for SMA: a dose-response study in mice and nonhuman primates.
Not available
S-EPMC4351452 | biostudies-literature
UnknownAAV9-MCT8 Delivery at Juvenile Stage Ameliorates Neurological and Behavioral Deficits in a Mouse Model of MCT8-Deficiency.
Not available
S-EPMC9469747 | biostudies-literature
UnknownOligodendrocytes contribute to motor neuron death in ALS via SOD1-dependent mechanism.
Not available
S-EPMC5081600 | biostudies-literature
UnknownIntracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease mice.
Not available
S-EPMC7887332 | biostudies-literature
UnknownThe C9orf72 protein interacts with Rab1a and the ULK1 complex to regulate initiation of autophagy.
Not available
S-EPMC4969571 | biostudies-literature
UnknownEarly postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease.
Not available
S-EPMC10080320 | biostudies-literature
Sort   by:  
 Page size