Data for modelling US projections of product approvals, patients treated, and product revenues for durable cell and gene therapies.
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ABSTRACT:
SUBMITTER: Young CM
PROVIDER: S-EPMC8844867 | biostudies-literature | 2022 Apr
REPOSITORIES: biostudies-literature
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Data for modelling US projections of product approvals, patients treated, and product revenues for durable cell and gene therapies.
Young Colin M CM Trusheim Mark M Quinn Casey C
Data in brief 20220203
The recent marketing approval of several durable gene and cell therapies (2017-2020), together with observations that 7,000 monogenic indications and many cancers were potential targets, led to concern about the potential economic impact of such therapies on the US healthcare system. Using a Markov chain Monte Carlo simulation model, driven stochastically by our estimates of the time in phase of clinical trials and each clinical trial phase probability of success, we forecast the pattern of futu ...[more]
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