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UnknownSomatic mosaicism in Menkes disease suggests choroid plexus-mediated copper transport to the developing brain.
Not available
S-EPMC3117432 | biostudies-literature
UnknownAML alters bone marrow stromal cell osteogenic commitment via Notch signaling.
Not available
S-EPMC10725948 | biostudies-literature
UnknownTranslational read-through of a nonsense mutation in ATP7A impacts treatment outcome in Menkes disease.
Not available
S-EPMC2917729 | biostudies-literature
UnknownGene, Stem Cell, and Alternative Therapies for SCA 1.
Not available
S-EPMC4981596 | biostudies-literature
UnknownTrihexyphenidyl rescues the deficit in dopamine neurotransmission in a mouse model of DYT1 dystonia.
Not available
S-EPMC6863078 | biostudies-literature
UnknownFetal Brain-directed AAV Gene Therapy Results in Rapid, Robust, and Persistent Transduction of Mouse Choroid Plexus Epithelia.
Not available
S-EPMC3696907 | biostudies-literature
UnknownRANKL Inhibition in Fibrous Dysplasia of Bone: A Preclinical Study in a Mouse Model of the Human Disease.
Not available
S-EPMC8408916 | biostudies-literature
UnknownLot-to-Lot Variation in Adeno-Associated Virus Serotype 9 (AAV9) Preparations.
Not available
S-EPMC6919242 | biostudies-literature
UnknownNanostring technology on Fibrous Dysplasia bone biopsies. A pilot study suggesting different histology-related molecular profiles.
Not available
S-EPMC8671863 | biostudies-literature
UnknownATP7A gene addition to the choroid plexus results in long-term rescue of the lethal copper transport defect in a Menkes disease mouse model.
Not available
S-EPMC3242653 | biostudies-literature
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