Sort   by:  
 Page size 
UnknownAge-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial.
Not available
S-EPMC4492302 | biostudies-literature
UnknownBibliometric analysis of global research trends in adeno-associated virus vector for gene therapy (1991-2022).
Not available
S-EPMC10739348 | biostudies-literature
UnknownSafety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial.
Not available
S-EPMC5351775 | biostudies-literature
UnknownThe Skeletal Muscle Environment and Its Role in Immunity and Tolerance to AAV Vector-Mediated Gene Transfer.
Not available
S-EPMC4515578 | biostudies-literature
UnknownEngineered AAV vector minimizes in vivo targeting of transduced hepatocytes by capsid-specific CD8+ T cells.
Not available
S-EPMC3606062 | biostudies-literature
UnknownUnraveling the Complex Story of Immune Responses to AAV Vectors Trial After Trial.
Not available
S-EPMC5649404 | biostudies-literature
UnknownAAV Vector Immunogenicity in Humans: A Long Journey to Successful Gene Transfer.
Not available
S-EPMC7054726 | biostudies-literature
UnknownA novel therapeutic strategy for skeletal disorders: Proof of concept of gene therapy for X-linked hypophosphatemia.
Not available
S-EPMC8550245 | biostudies-literature
UnknownClinical outcomes and temporal trends of immunological and non-immunological rare diseases in adult kidney transplant.
Not available
S-EPMC8600810 | biostudies-literature
UnknownEmerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for Hemophilia.
Not available
S-EPMC8199697 | biostudies-literature
Sort   by:  
 Page size